Traejen spent hours a day on dialysis after a failed kidney transplant, until a new approach cured his FSGS and helped him get his life back.


Traejen spent hours a day on dialysis after a failed kidney transplant, until a new approach cured his FSGS and helped him get his life back.
Shriya is one in a million. For starters, she’s a 9-year-old girl who will talk… Read more »
Matthew Porteus, MD, PhD, is leading clinical research for CRISPR at Lucile Packard Children’s Hospital and hopes to launch Stanford’s first clinical trial of CRISPR next year.
Using stem cells and gene therapy to treat or cure disease may still sound like science fiction, but it is moving closer and closer to fact.
Recently, Stanford pediatric cardiologist Marlene Rabinovitch, MD, and her team published new research that advances their quest to understand a serious — and very puzzling — lung disease.
For years, pediatric cardiologists have been trying to understand the origin of a puzzling congenital defect that creates a spongy texture in the heart muscle wall. Now, Stanford researchers have shown that they can use stem cell techniques to turn donated skin and blood cells from real patients into a useful tool for figuring out how the disease gets started.
Stanford recently launched the world’s first stem-cell based trial aimed at a devastating skin disease called epidermoloysis bullosa. Physicians from our dermatology team are trying to correct a faulty gene in the skin cells of patients with a severe form of the condition, which causes large, painful wounds and currently has no cure.
New mothers looking to make a big difference for families facing life-threatening medical conditions have… Read more »