Swimming and Snowmen: A New Life for Preteen With Sickle Cell Disease
After gene therapy freed Aba from the chronic pain caused by sickle cell disease, she’s imagining a new life without limitations.
After gene therapy freed Aba from the chronic pain caused by sickle cell disease, she’s imagining a new life without limitations.
A clinical trial testing a different gene therapy approach for sickle cell disease will soon be expanding to younger patients.
After living with severe hemophilia B for decades, Julian hasn’t had a bleed or an infusion since his gene therapy at Stanford Medicine Children’s Health.
For Karar, living with beta thalassemia meant monthly infusions to keep his energy up, until gene therapy cured him.