New Gene Correction Clinical Trial for Sickle Cell Disease Expanding to Children as Young as 12
A clinical trial testing a different gene therapy approach for sickle cell disease will soon be expanding to younger patients.
Posts Tagged with
gene therapy
Gene Therapy Helps Father With Hemophilia Live an Active Life
After living with severe hemophilia B for decades, Julian hasn’t had a bleed or an infusion since his gene therapy at Stanford Medicine Children’s Health.
Gene Therapy Cures Soccer-Loving Boy of Beta Thalassemia
For Karar, living with beta thalassemia meant monthly infusions to keep his energy up, until gene therapy cured him.
